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FDA blocks much-anticipated BioMarin hemophilia gene therapy

by AP Medical Writer
| August 20, 2020 12:06 AM

FAIRLESS HILLS, PA (AP) — Investors fled drug developer BioMarin in droves on Wednesday, driving shares down by a third after U.S. regulators rejected the company’s potentially game-changing hemophilia A gene therapy over concerns it might not really be a one-and-done lifetime treatment.

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